Paediatric Diseases Working Party (PDWP)
Study type:
Study number:
8417020
Type of treatment:
Diseases:
Short title:
Primary objective:
Primary objective is to determine the effectivity of eculizumab treatment in HSCT-TMA in children.The goal is to collect the unpublished real-life experience of eculizumab use that may help the current practice and shape the future research.
Key inclusion criteria:
- Age 0-18yrs
- Allogeneic haematopoietic stem cell transplantation recipient
- HSCT-TMA diagnosed according to any of the 6 criteria listed (defined in the questionnaire, attached))
- Treatment with eculizumab
- Informed consent given for EBMT registry data collection
- Allogeneic haematopoietic stem cell transplantation recipient
- HSCT-TMA diagnosed according to any of the 6 criteria listed (defined in the questionnaire, attached))
- Treatment with eculizumab
- Informed consent given for EBMT registry data collection
Country:
Principal investigator:
Peter Svec
EBMT Study coordinator:
Arnaud Dalissier