Paediatric Diseases Working Party (PDWP)
Study type:
Study number:
Type of treatment:
Diseases:
Short title:
Primary objective:
Collaboration EWOG EBMT and some UK centers
Key inclusion criteria:
Patients affected with autosomal dominant RUNX1 mutation related disease
Country:
Principal investigator:
Giovanna Lucchini
EBMT Study coordinator:
Arnaud Dalissier
Study coordinator email:
arnaud.dalissier@upmc.fr